Clinical Trials and Studies
Some clinical trials have suspended enrollment until further notice due to COVID-19 considerations.
Pediatric Neurological Disorders
- Drug Treatment Study for Boys with Duchenne Muscular Dystrophy
- Duchenne Muscular Dystrophy Treatment Study
- Efficacy, Safety and Tolerability of RO5186582 in Adults and Adolescents with Down Syndrome
- Expressive Language Sampling as an Outcome Measure
- Extension Study of Ataluren Treatment for Nonsense Mutation Dystrophinopathy
- Fragile X Study: Premutation Carriers
- Nonsense Mutation Dystrophinopathy and Ataluren Treatment Study
- Treatment Study for Boys with Duchenne Syndrome